The month of March has been declared Amyloidosis Awareness Month in the City of Medicine Hat, to encourage residents to educate themselves on this potentially fatal condition. Amyloidosis is a rare ...

Alnylam Canada ULC is pleased to announce it has received a positive recommendation from Canada's Drug Agency (CDA) for the public reimbursement of its RNAi therapeutic, AMVUTTRA®.1 In December 2025, ...

We are very pleased to have aligned with the FDA on the path forward for our MAGNITUDE clinical trial, with measures designed ...

Networked models of care have the potential to provide better access to specialist care for rare diseases in the NHS. The government committed to establishing an innovative networked model of care for ...

“There was actually no treatment to slow down the process or the progression of the disease. The only treatment that was ...

HAELO Phase 3 clinical data for lonvo-z in HAE expected by mid-2026; BLA submission in second half of 2026; anticipated U.S. launch in first half ...

These drugs reduce production of the abnormal transthyretin protein in the liver, which is responsible for many cases of cardiac amyloidosis. Doctors report that the medications have led to fewer ...

Eric Dane, known for his roles on “Grey’s Anatomy” and “Euphoria,” died this week from amyotrophic lateral sclerosis at age 53. The fatal nervous system disease, also known as Lou Gehrig’s disease, ...

Patients are now being identified earlier than ever, and new drugs approved by the FDA are prolonging their lives significantly.

Jayashri Kulkarni receives funding from the National Health and Medical Research Council as a Leadership Level 3 Investigator Grant, and has received clinical trials funding from pharmaceutical ...

Cardiac amyloidosis is a systemic disorder that affects the heart and can also affect other organs such as the kidneys and nervous system.

Catherine O’Hara, the Emmy‑winning star of Home Alone, Schitt’s Creek and Beetlejuice, died on January 30 at the age of 71 after suffering a pulmonary embolism, according to her Los Angeles County ...