Early recognition by clinicians is essential. When youth present with repeated vomiting, abdominal pain, or unexplained ...

Please provide your email address to receive an email when new articles are posted on . Most patients with newly diagnosed high-risk myelodysplastic syndrome do not receive guideline-recommended ...

Nephrotic syndrome is a clinical entity defined by heavy proteinuria, hypoalbuminemia, hyperlipidemia, and edema, stemming from various glomerular diseases. Diagnosis requires a comprehensive ...

Walker Burger always loved baseball, but attending the games of his favorite team, the Atlanta Braves, used to be a physical challenge. In fact, every form of exercise was difficult. Burger, 35, has a ...

The FDA has granted accelerated approval for the elamipretide injection, the first treatment for Barth syndrome in patients weighing at least 30 kg. Barth syndrome is a life threatening disease of the ...

The FDA on Friday granted accelerated approval to elamipretide (Forzinity) as the first treatment for the ultra-rare Barth syndrome, which affects approximately 150 Americans. Elamipretide once-daily ...

After a tumultuous journey filled with delays and rejection, the FDA has approved Stealth BioTherapeutics’ treatment for the ultrarare disease Barth syndrome, marking the peptide as the first therapy ...

The epidemiology of tumor lysis syndrome is evolving with the introduction of newer therapies. The occurrence of tumor lysis syndrome has become a less predictable but increasingly important aspect of ...

Reclassifying marijuana from a Schedule I to a Schedule III drug could be beneficial for science but may also be seen as a safety endorsement for heavy use. A 2024 study found that daily or near-daily ...

Researchers at The Hospital for Sick Children (SickKids) have uncovered a promising new therapeutic target for Barth syndrome, a rare genetic condition with no current cure. Barth syndrome is an ...

Mr. Humphreys is a professor of psychiatry at Stanford University and served as senior drug policy adviser in the Obama administration. He is a member of the board of Indivior, which manufactures ...

What can you tell me about restless leg syndrome? Over the past year or so I’ve developed an uncontrollable urge to move my legs because of an annoying tingling sensation, and it’s keeping me awake at ...