On June 2, 2025, uniQure shared that they’re aligned with the FDA about moving forward with their HTT-lowering gene therapy, AMT‑130. If the next round of results from their ongoing trial continues to ...

Huntington’s disease research news. In plain language. Written by scientists. For the global HD community.

The brain has plans in place when fires break out. Normally, a molecule called PKD1 rushes in to the rescue, but in ...