These drugs reduce production of the abnormal transthyretin protein in the liver, which is responsible for many cases of cardiac amyloidosis. Doctors report that the medications have led to fewer ...

New drugs approved by the FDA are prolonging the lives of those affected.

An amyloidosis diagnosis can take upwards of 2 years.Initial symptoms often are nondescript, and irreversible organ damage frequently occurs before disease confirmation.

Transthyretin cardiac amyloidosis (ATTR-CA) is a frequent cause of heart failure (HF) in older Black individuals, particularly in the oldest men, the prospective SCAN-MP study affirms. The highest ...

Networked models of care have the potential to provide better access to specialist care for rare diseases in the NHS. The government committed to establishing an innovative networked model of care for ...